×

Tag: AAV

Nanoparticles in blood
Scientists have successfully tested a new nanoparticle-based delivery system for CRISPR kits, achieving drastic improvements in mouse models of glioblastoma and ovarian cancer [1]. A gift from our single-cell ancestors CRISPR gene editing technology has been widely hailed as a potential game changer in medicine, including anti-cancer therapy. CRISPR’s ability to permanently disrupt tumor survival...
Image of someone editing DNA
A gene therapy treatment can ameliorate the loss of motor function and muscle strength in old mice, offering elderly people hope for continuing their active lives. DOK7 is crucial for muscle function Declining motor function is common with aging and can significantly reduce the quality of life. This decline occurs at least in part due...
Colombia
Recently, Libella Gene Therapeutics has announced that it will be running a patient-paid trial in Colombia with an eye-watering $1 million USD price tag on enrollment. Patient-paid trial likely to cause backlash The topic of patient-paid trials often stirs up considerable debate among the research community, regulatory authorities, and the general public, with many people...